Sickle cell gene therapies offer new hope, but access remains a major challenge
FDA-approved gene therapies for sickle cell disease offer a chance to help patients, but factors including cost and access have slowed their use.
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FDA-approved gene therapies for sickle cell disease offer a chance to help patients, but factors including cost and access have slowed their use.
Fantastic Fest, the annual Austin-based celebration of genre filmmaking, has announced top honors for its films in competition. “Our winning films embody distinctive and powerful voices from a wide range of cultures, and the exciting new generation of talent shaping the future of genre cinema,” Annick Mahnert, director of programming, said in a statement. “It […]
A newly discovered communication system in the microscopic “antennae” of cells may help explain how some congenital heart defects develop. When genetic mutations disrupt this system, the effects may extend beyond the heart to organs including the brain, kidneys, and skeleton.